2nd Medical Affairs & Rare Disease
West Coast

Cross Functional Collaboration in Rare Disease:
Breaking Down Silos to Identify Solutions

August 24-25, 2020

San Diego, CA

Event Overview

Dynamic Global Events is excited to announce the 2nd Annual Medical Affairs in Rare Diseases Forum on the west coast. This is a CE/CME- accredited conference for life sciences professionals in rare and ultra-rare diseases.
 
Join with thought leaders and decision makers to become a strong and collaborative medical affairs partner who will work collaboratively to drive better medical strategies affecting therapy research (orphan drugs, gene therapies, biosimilars/biologics, T-Cell), pharmacovigilance, clinical trials, HEOR, launches, medical communications, domestic/international brand plans, drug/patient safety . This forum will provide actionable insights into best practices for building and leading high-performing multi-stakeholder teams across functions, geographies, therapeutic areas and organizations to solve problems and identify solutions in rare disease.

Wyndham Bayside San Diego

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1355 N Harbor Dr.
San Diego, CA 92101
(619) 232-3861

Hotel Website

About the Chairperson

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Dr. Matthew T. Roe has been a faculty member at Duke University School of Medine and the Duke Clinical Research Institute (DCRI) since 1999. As a senior investigator at the DCRI, he has been the principal investigator for numerous phase II-IV cardiovascular clinical trials and is currently a co-principal investigator for the ADAPTABLE trial—the first large-scale pragmatic trials being conducted in the PCORnet network. He has also served in leadership roles for several observational registries focusing upon the treatment and outcomes of patients with cardiovascular disease and has served as the Director of the DCRI Clinical Research Fellowship since 2010.

Featured Speakers

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Craig Lipset

Head of Clinical Innovation
Pfizer

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Jeff Kingsley

Chief Executive Officer
IACT Health 

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Dawn Anderson

Managing Director, Life Sciences Strategy and Operations, R&D Practice
Deloitte

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Ross Friedberg

General Counsel & Chief Privacy Officer
Doctor on Demand

Top Reasons to Attend

  1. Learn best practices to cultivate multi-stakeholder professional relationships and build internal cross-functional teams to improve rare disease patient outcomes through collaboration
  2. Discuss competitive advantages created with strategic partnerships between pharmaceutical companies and university medical centers
  3. Gain insights into best practices for FDA approval; OR into FDA regulations regarding biosimilars and Gene therapy for rare
  4. Explore new developments in translational medicine, HERO in rare, drug pipelines for biosimilars/gene therapies/T-cell therapies, real world evidence for the FDA, off-label uses for orphan drugs
  5. Learn about digital tools for the benefit-risk optimization of medicines

Attendee Profile

This Conference is Designed for Life Science Professionals responsible for:

  • Rare Disease
  • Orphan Drugs
  • Biosimilars/Biologics
  • Gene Therapy
  • T-Cell Studies
  • Medical Affairs
  • Clinical Affairs
  • Quality Assurance
  • Pharmacovigilance
  • Drug/Patient Safety
  • Regulatory Affairs
  • Compliance
  • Product Development
  • Product Launch
  • Health Economics and Outcomes Research/HEOR
  • Reimbursements
  • Medical Messaging
  • Marketing
  • Clinical Research Organizations (CROs)
  • eClinical Technologies
  • Data Management/Integration
  • Patient Engagement
  • Patient Advocacy
  • Medical Science Liaisons (MSLs)
  • KOL/Thought Leader Relations/Engagement
  • Cross Functional Team Management
  • Strategic Planning
  • Medical Publication/Digital Communication Planning
  • University/Medical School Rare Disease Research

Monday

August 24th, 2020 | Day 1

8:00 AM - 9:00 AM

Registration & Continental Breakfast

9:00 AM - 9:15 AM

Conference Opening Remarks

9:15 AM - 10:00 AM

Medical Affairs as the Strategic Driver within an Organization

10:00 AM - 10:45 AM

Medical Affairs Do’s and Don’ts – Transitioning from a Small Biotech to a Large Biopharma Company

Oscar Seguardo, MD, Ph.D - Chief Medical Officer
ASC THERAPEUTICS

10:45 AM - 11:00 AM

Morning Networking Break

11:00 AM - 12:00 PM

Collaborative Private/Public Partnerships for Real World Evidence Collection and Expanded Access to Rare Disease Therapies

Wendy White - Chairman
GLOBAL GENES and Co-Founder, RAREITI

Natalie Douglas - Vice Chairman
GLOBAL GENES and Co-Founder, RAREITI

12:00 PM - 1:00 PM

Networking Lunch

1:00 PM - 1:45 PM

Collaborating Around Rare Disease

Jon Kaskey - Regional Vice President, Business Partnerships
WITHIN3

1:45 PM - 2:45 PM

PANEL: Rare Disease Clinical Research: Literacy, Diversity, Engagement, Technology and Retention

Joan A. Chambers - Senior Director, Marketing and Outreach
CENTER FOR INFORMATION & STUDY ON CLINICAL RESEARCH PARTICIPATION (CISCRP)

Harsha Rajasimha, MS, Ph.D - Founder and CEO
JEEVA INFORMATICS SOLUTIONS INC.

2:45 PM - 3:00 PM

Afternoon Networking Break

3:00 PM - 4:00 PM

Creating Strategic Plans for Cross Functional Collaboration and Growth

Andy Overmyer - Head of Global Business Operations
AKCEA THERAPEUTICS

4:00 PM - 4:45 PM

PANEL: The Impact of Technology on Patient Engagement

  • Recruiting
  • Hybrid and Virtual Clinical Trials
  • Digital Marketing and Convenience-based Applications

Joan A. Chambers - Senior Director, Marketing and Outreach
CENTER FOR INFORMATION & STUDY ON CLINICAL RESEARCH PARTICIPATION (CISCRP)

Harsha Rajasimha, MS, Ph.DFounder and CEO
JEEVA INFORMATICS SOLUTIONS INC.

4:45 PM - 5:00 PM

Day 1 Closing Remarks

Tuesday

August 25th, 2020 | Day 2

8:00 AM - 9:00 AM

Registration & Continental Breakfast

9:00 AM - 9:15 AM

Recap of Day 1 & Day 2 Opening Remarks

9:15 AM - 10:00 AM

HEOR and Determining the Value of Rare Disease Therapies

10:00 AM - 10:45 AM

Patient Centricity and Including the Patient Voice in Clinical Trials

10:45 AM - 11:00 AM

Morning Networking Break

11:00 AM - 12:00 PM

PANEL: Expanding and Changing Role of MSLs in Rare Disease

12:00 PM - 1:00 PM

Networking Lunch

1:00 PM - 1:45 PM

Sponsor Session Topic TBD

Robert Consalvo - Director of Strategic Commercial Engagement
H1 INSIGHTS

1:45 PM - 2:30 PM

Access to Rare Disease Therapies – Fast Tracking, Early Access and Expanded Access

2:30 PM - 2:45 PM

Afternoon Networking Break

2:45 PM - 4:45 PM

MEDICAL AFFAIRS RARE DISEASE CASE STUDY PRACTICUM
BEST PRACTICES FOR BREAKING DOWN SILOS TO IDENTIFY SOLUTIONS

  • Actionable Implications to Achieve Clinical Development, Product Launch Goals, Drug Safety and Favorable Outcomes
  • Building High-performing Multi-stakeholder Teams
  • Leading Internal Project Teams Across Functions, Geographies and Therapeutic Areas
  • Collaborating Across Organizations -- Science, Business and Non-profits

Thomas Lester - Executive Director Program Management
AUDENTES THERAPEUTICS

Steven G. Rizk, PharmD, JD - Senior Director -  Medical Strategy
RYPE HEALTH

4:45 PM - 5:00 PM

Day 2 Closing Remarks

FEATURED SPEAKERS

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Oscar Segurado

ASC Therapeutics

Chief Medical Officer

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Israel Gutierrez

Geron Corporation

Vice President, Pharmacovigilance and Drug Safety

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Joan A. Chambers

The Center for Information & Study on Clinical Research Participation (CISCRP)

Senior Director, Marketing & Outreach

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Michael Forstner

PrimeVigilance

Senior Vice President and Head of Pharmacoepidemiology and Risk Management

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Sheila Bose

SB Lifesciences Consulting, Inc

President

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Christine Von Raesfeld

More Than Lupus

Patient Advocate and Board Member

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Angela Ramirez Holmes

Cal Rare

Founder/President

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Tom Lester

Audentes Therapeutics

Executive Director Program Management

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Steven G. Rizk

Rype Health

Senior Director Medical Strategy

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Maureen McArthur Hart

Global Genes

Director, Research

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Andy Overmyer

Akcea Therapeutics

Head of Global Business Operations

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Wendy White

GLOBAL GENES

Chairman

Co-Founder, RAREITI

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Natalie Douglas

GLOBAL GENES

Vice Chairman

Co-Founder, RAREITI

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Harsha K. Rajasimha

Jeeva Informatics Solutions Inc.

Founder and CEO

Founder Chairman, Indo US Organization for Rare Diseases

CONFERENCE REGISTRATION


ATTENDEE PRICING

* SUPER EARLY BIRD *

Before 4/24/20

$1,596

EARLY BIRD

Before 6/26/20

$1,796

STANDARD

Register Before Event

$1,996

ON-SITE

Register at Event

$2,196

VIRTUAL LIVE STREAM

Register Anytime

$896

Register 2 Attendees, Get 1 Complimentary Registration*!

Interested in sending groups of 7 or more? Contact us directly for pricing.

EVENT SPONSORS



SPONSOR THIS EVENT

Contact Amy Chapman at (561) 571-7687
or achapman@dgeconfs.com


MEDIA PARTNERS

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PREMIER MEDIA PARTNER